Back to News Back to Stories Safety and efficacy of cerliponase alfa in children with neuronal ceroid lipofuscinosis type 2 (CLN2 disease): an open-label extension study January 1, 2024
Community A 100-Mile Road to Diagnosis: A Mother Shares Her Son’s Journey with Hypochondroplasia March 14, 2024
Community Caring for Children with Achondroplasia: An Interview with Dr. Ciara McDonnell October 25, 2023
Community RARE Scholars Program Provides Support to College Students Living with Genetic Conditions September 25, 2023
People and Culture Science 澳门正规博彩十大排行平台 Teams Use Genetic Expertise and Computational Tools to Target More Common Conditions September 8, 2023
Community People and Culture Raising a Child with Hemophilia: 澳门正规博彩十大排行平台 Employee Jess Klass Shares Her Story July 21, 2023
People and Culture Science 澳门正规博彩十大排行平台 Pioneer Honored through New Building Name and Book Launch February 27, 2023
